Rare Disease Research

Our Goal

Alexion Pharmaceuticals, Inc. is committed to researching rare diseases and investigating potential new treatments that have the possibility of transforming patients' lives.

Most patients with severe and life-threatening rare diseases live with no effective treatment options and no hope. Alexion's clinical trials investigate potential new therapies that may offer hope to people who haven't yet found a therapy that works or that they can tolerate.

*For more information on how Alexion collects, uses and protects your personal information, please review our Privacy Notice.

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