Frequently asked questions (FAQs)
Clinical trials can seem complex, but understanding the process shouldn’t be. Explore quick, clear answers to common questions from patients and caregivers. Whether you’re considering participation or simply want to learn more, these FAQs are here to help you feel informed and confident.
Understanding clinical trials
Clinical trials can focus on different things. Some test brand-new medicines, others look at new ways to use treatments that are already approved, and some study ways to manage symptoms or improve daily life. Each type helps doctors and scientists learn more and develop better care for patients.
In a single-blind clinical trial, participants don’t know whether they’re receiving the investigational treatment or a placebo. In a double-blind trial, neither participants nor trial staff know. This helps prevent bias and ensures the results are scientifically accurate.
A placebo looks like the investigational medicine but doesn’t contain active ingredients. It helps researchers compare results and determine whether the investigational treatment works as expected. Participants are always informed if a placebo is used in a clinical trial, though they may not know if they are receiving the placebo or not.
Before you decide whether to participate, the trial team will walk you through an informed consent process. This discussion explains the trial’s purpose, procedures, potential risks and benefits, and your rights as a participant. Signing the consent form confirms you understand the details and choose to take part voluntarily.
There is no cost to participate in an Alexion clinical trial. Trial-related procedures, tests, and treatments are typically provided at no charge. In many cases, participants may receive reimbursement for time and travel related to trial visits.
Your safety in every clinical trial
All medical treatments carry some level of risk, and every trial includes detailed information about potential side effects. Before joining, you’ll review these details with the trial team during the informed consent process. You will have time to ask questions and decide what’s right for you.
Your safety is monitored throughout the trial by the study investigator (lead doctor), the trial staff, and an independent ethics committee. In many cases, a safety monitoring board also reviews data regularly to ensure ongoing participant protection.
Practical details
Every trial is different. Some trials last a few weeks, while others may continue for several months or years. Your trial team will explain the schedule of visits and how often you’ll need to come to the trial site.
Depending on the clinical trial, you may or may not be able to continue your current treatment. Your doctor can discuss this with you.
Participation is voluntary, and you can leave the trial at any time. You may be asked to complete a final visit with the trial team should you choose to leave a trial before it's complete.
Privacy and data protection
Protecting your privacy is one of Alexion’s top priorities. All personal and medical information collected during a trial is kept confidential and stored securely. Your data is anonymized (your name and identifying details are removed) and used only for approved research purposes in compliance with global privacy laws such as the General Data Protection Regulation (GDPR) and the Health Insurance Portability and Accountability Act (HIPAA).
