Find a clinical trial
Our trials focus on advancing treatments for rare diseases with the goal of bringing new hope, options, and understanding to patients and families worldwide. Explore Alexion’s current clinical trials and discover how you or a loved one may be able to take part.
Our research areas
Alexion is committed to investigating rare conditions across multiple therapeutic areas. Each area represents a focused effort to understand complex diseases and develop innovative therapies that can change lives.
Rare bone
Developing targeted therapies to help patients with rare bone diseases live stronger, healthier lives.
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Rare cardiology
Advancing potential treatments for rare heart conditions to improve health and daily living.
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Rare endocrine disorders
Exploring new approaches to improve care for people living with rare endocrine conditions.
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Rare hematology
Creating therapies that address rare blood disorders and help patients live fuller, healthier lives.
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Rare nephrology
Pioneering treatments to improve outcomes for patients with rare kidney conditions.
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Rare neurology
Working to advance potential therapies for rare neurological conditions that affect daily life.
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Rare tumours
Researching new approaches to help improve outcomes for people with rare cancers.
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Healthy volunteers
Conducting studies to support research and advance care for rare disease communities.
ExploreRecruiting trials
Rare hematology
A Phase 1b/2 Study of CAR T Cell Therapy Targeting CD19 and BCMA in Participants With Relapsed or Refractory AL Amyloidosis. (ALACRITY)
More informationRare Cardiology
ALXN2350 in Adult Participants With BAG3-Associated Dilated Cardiomyopathy (DCMRestore)
More informationRare Nephrology
Study of Ravulizumab in Pediatric Participants With Primary IgAN (ICAN Jr.)
More informationRare Nephrology
Study of ALXN1920 in Adult Participants With Primary Membranous Nephropathy (PMN) (AUTUMN)
More informationRare hematology
Safety and Efficacy of Tarperprumig in Adult Participants With Anti-Neutrophil Cytoplasmic Antibody (ANCA)-Associated Vasculitis (I TRANSCEND)
More informationRare Nephrology
Double-blind, Randomized, Placebo-controlled, Multicenter Study to Evaluate the Efficacy and Safety of Ravulizumab Administered Intravenously in Adult Participants at High Risk of Delayed Graft Function After Kidney Transplantation (AWAKE)
More informationRare hematology
